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Clinical Trials for Tyrosinemias

  • Bio Equivalency 20 Mgm Orfadin and 20 Mgm of Nitisonine
  • Bioequivalence Study of Two Nitisinone Formulations Compared to Orfadin
  • Bioequivalence Study of Two Oral Nitisinone Formulations to Treat Hereditary Tyrosinemia (HT-1)
  • Bioavailability Food-Effect Study of an Oral Nitisinone Formulation to Treat Hereditary Tyrosinemia (HT-1)
  • Efficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1
  • Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care
  • Taste and Palatability of Orfadin Suspension
  • Study of NTBC for Tyrosinemia I
  • Phase II Study of the Enzyme Inhibitor NTBC for Tyrosinemia Type I
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