Overview

Study of NTBC for Tyrosinemia I

Status:
Completed
Trial end date:
2006-09-01
Target enrollment:
Participant gender:
Summary
OBJECTIVES: I. Assess the safety and efficacy of NTBC in children with tyrosinemia I. II. Evaluate the effects of NTBC on survival, rate of neurologic crises, improvement in renal tubular damage, reduction in the need for liver transplantation, and reduction in the development of hepatocarcinoma in these patients.
Phase:
N/A
Details
Lead Sponsor:
University of Washington