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Clinical Trials for Hyperargininemia

  • Pegzilarginase in Subjects <24 Months Old With Arginase 1 Deficiency
  • A Study of Safety of Weekly Subcutaneous Pegzilarginase in Subjects With Arginase 1 Deficiency
  • Efficacy and Safety of Pegzilarginase in Patients With Arginase 1 Deficiency
  • A Study of AEB1102 (Pegzilarginase) in Patients With Arginase I Deficiency
  • A Phase 1/2 Study of AEB1102 in Patients With Arginase I Deficiency
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