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Clinical Trials for Congenital, Hereditary, and Neonatal Diseases and Abnormalities

  • Efficacy and Safety of SIL-8301 for Control of Hemolysis in a Uniform Sickle Cell Disease Endotype
  • Azithromycin and Ampicillin for Late PPROM
  • Ascending Doses of Crofelemer Powder for Oral Solution in Pediatric Microvillus Inclusion Disease (MVID)
  • Nasal High Frequency in Preterm Neonates
  • Melatonin for Pulmonary Hypertension in Full Term Neonates
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