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Clinical Trials for Canavan Disease

  • rAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease
  • Oral Glyceryl Triacetate (GTA) in Newborns With Canavan
  • Lithium and Acetate for Canavan Disease
  • GTA-Glyceryltriacetate for Canavan Disease
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