Umbilical Cord Blood Transfusion in Progeria Syndrome
Status:
Completed
Trial end date:
2020-06-01
Target enrollment:
Participant gender:
Summary
This is a pilot study on safety and efficacy of umbilical cord blood therapy for patients
with Hutchinson Gilford Progeria syndrome (HGPS). This is an 1 year trial with 3 IV infusions
(4 months apart from each infusion) of umbilical cord blood units with oral Sirolimus to see
the safety and efficacy.