Overview

Trikafta for Patients With Non-cystic Fibrosis Bronchiectasis

Status:
Recruiting
Trial end date:
2024-06-01
Target enrollment:
Participant gender:
Summary
Study participants with non-cystic fibrosis bronchiectasis will be given Trikafta for four weeks. The researchers will monitor clinical endpoints, quality of life, and weight. Additionally, cutaneous punch biopsy material will be collected from each participant to test cellular response to Trikafta.
Phase:
Phase 4
Details
Lead Sponsor:
Emory University
Collaborator:
The Marcus Foundation, Inc.
Treatments:
Elexacaftor
Ivacaftor