Trial on Safety and Efficacy of Velmanase Alfa Treatment in Pediatric Patients With Alpha-Mannosidosis
Status:
Completed
Trial end date:
2020-07-01
Target enrollment:
Participant gender:
Summary
The main objectives of the study are to evaluate safety and efficacy of repeated treatment
with recombinant human alfa-mannosidase of patients with alfa-mannosidosis aged less than 6
years