Overview Targeted Busulfan, Fludarabine Conditioning Regimen for Hematopoietic Stem Cell Transplantation in GRD Status: Recruiting Trial end date: 2021-11-01 Target enrollment: Participant gender: Summary To evaluate the outcome of hematopoietic stem cell transplantation using targeted busulfan, fludarabine conditioning regimen in genetic rare disease Phase: Phase 1/Phase 2 Details Lead Sponsor: Seoul National University HospitalTreatments: BusulfanFludarabineFludarabine phosphate