Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With Phenylketonuria
Status:
Not yet recruiting
Trial end date:
2025-12-01
Target enrollment:
Participant gender:
Summary
This is a Phase 3 open-label randomized controlled study enrolling approximately 54
adolescents with PKU. The study is designed to assess the safety and efficacy of pegvaliase
injections.