Study to Evaluate Patients With Cerebrotendinous Xanthomatosis
Status:
Recruiting
Trial end date:
2023-03-01
Target enrollment:
Participant gender:
Summary
The study is made up of two cohorts: a randomized double-blind crossover (placebo withdrawal
with rescue) study among patients ≥ 16 years of age (adult cohort) and an open-label dose
titration study among pediatric patients ≥1 month and <16 years of age (pediatric cohort)