Overview

Study to Evaluate DT-216 in Adult Patients With Friedreich Ataxia

Status:
Recruiting
Trial end date:
2022-12-31
Target enrollment:
Participant gender:
Summary
The purpose of this study is to evaluate the safety, tolerability, pharmacokinetic and pharmacodynamic effects of intravenous DT-216 in adult patients with Friedreich Ataxia. This single ascending dose study is randomized, double-blind, placebo-controlled.
Phase:
Phase 1
Details
Lead Sponsor:
Design Therapeutics