Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53)
Status:
Recruiting
Trial end date:
2024-12-01
Target enrollment:
Participant gender:
Summary
The main objective of this study is to evaluate the efficacy of Viltolarsen compared to
placebo in Duchenne muscular dystrophy (DMD) patients amenable to exon 53 skipping.