Overview

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Status:
NOT_YET_RECRUITING
Trial end date:
2027-08-08
Target enrollment:
Participant gender:
Summary
The purpose of this study is to evaluate the safety, pharmacodynamics (PD), and exploratory clinical efficacy of S-606001 in adult participants with LOPD as an add-on to ERT.
Phase:
PHASE2
Details
Lead Sponsor:
Shionogi