Study of Recombinant Human N-acetylgalactosamine 4-sulfatase (rhASB) in Patients With MPS VI
Status:
Completed
Trial end date:
2004-03-01
Target enrollment:
Participant gender:
Summary
The purpose of the study is to evaluate the ability of rhASB versus placebo to enhance
endurance in patients with Mucopolysaccharidosis VI (MPS VI), as evidenced by an increase in
the number of meters walked in the 12 minute walk test at Week 24 compared with baseline.