Overview

Study of Ravulizumab in Pediatric Participants With HSCT-TMA

Status:
Recruiting
Trial end date:
2024-02-01
Target enrollment:
Participant gender:
Summary
This study will evaluate the safety, efficacy, pharmacokinetics, and pharmacodynamics of ravulizumab administered by intravenous infusion to pediatric participants, from 1 month to < 18 years of age, with HSCT-TMA. The treatment period is 26 weeks, followed by a 26-week off-treatment follow-up period.
Phase:
Phase 3
Details
Lead Sponsor:
Alexion Pharmaceuticals
Treatments:
Ravulizumab