Overview

Stem Cell Transplant w/Laronidase for Hurler

Status:
Completed
Trial end date:
2012-11-01
Target enrollment:
Participant gender:
Summary
The investigators hypothesize that weekly infusions of Laronidase ERT for 10-12 weeks prior to transplant and 8 weeks following transplant will result in a reduction of glycosaminoglycans (GAG) burden that is associated with decreased complications following transplant.
Phase:
Phase 2
Details
Lead Sponsor:
Masonic Cancer Center, University of Minnesota