Sapropterin on Cognitive Abilities in Young Adults With Phenylketonuria
Status:
Terminated
Trial end date:
2014-11-01
Target enrollment:
Participant gender:
Summary
This is a Phase 2a multicenter, double-blind, placebo-controlled, randomized, 2-arm pilot
trial designed to assess the effect of sapropterin on cognitive abilities in young adults
with Phenylketonuria (PKU) over a 26-week treatment period.