Overview

Safety and Efficacy of Miglustat in Chinese NPC Patients

Status:
Active, not recruiting
Trial end date:
2022-05-30
Target enrollment:
Participant gender:
Summary
This is a prospective, multi-center, open-label, non-randomized, single-arm Phase IV confirmatory study. Approximately 19 subjects with Niemann Pick Type C disease (NPC) will be enrolled in this study. The study will be conducted at 2 sites in China.
Phase:
Phase 4
Details
Lead Sponsor:
Actelion
Treatments:
1-Deoxynojirimycin
Miglustat