Safety and Efficacy of Clenbuterol in Individuals With Late-onset Pompe Disease and Receiving Enzyme Replacement Therapy
Status:
Completed
Trial end date:
2016-09-02
Target enrollment:
Participant gender:
Summary
Funding Source- FDA OOPD
The purpose of this study is to investigate the safety and efficacy of clenbuterol on motor
function in individuals with late-onset Pompe disease (LOPD) who are treated with enzyme
replacement therapy (ERT).