Safety and Efficacy of Albuterol in Individuals With Late-onset Pompe Disease
Status:
Completed
Trial end date:
2016-12-16
Target enrollment:
Participant gender:
Summary
In this study the study team proposes to investigate the efficacy of albuterol on motor
function of individuals with Late Onset Pompe Disease (LOPD) who are receiving enzyme
replacement therapy, given albuterol was well-tolerated in patients with Late Onset Pompe
Disease.