Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome
Status:
Completed
Trial end date:
2015-05-31
Target enrollment:
Participant gender:
Summary
The purpose of this study is to evaluate the effects of EPI-743 in children with Leigh
syndrome on disease severity, neuromuscular function, respiratory function, disease morbidity
and mortality and disease associated biomarkers.