Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular Dystrophy
Status:
Completed
Trial end date:
2018-03-23
Target enrollment:
Participant gender:
Summary
The primary objective of this study is to explore safety and tolerability of eteplirsen in
participants with advanced stage Duchenne muscular dystrophy (DMD) who are amenable to exon
51 skipping.