Overview

Rapamycin Treatment for Activated Phosphoinositide 3-Kinase δ Syndrome

Status:
Recruiting
Trial end date:
2022-11-30
Target enrollment:
Participant gender:
Summary
The purpose of this proposed research is to evaluate the efficacy and safety of the rapamycin therapy in patients with activated phosphoinositide 3-kinase δ syndrome (APDS).
Phase:
Phase 1/Phase 2
Details
Lead Sponsor:
Children's Hospital of Fudan University
Treatments:
Sirolimus