Pilot Study of Metformin for Patients With Fanconi Anemia
Status:
Completed
Trial end date:
2020-10-09
Target enrollment:
Participant gender:
Summary
This is a single institution, open-label, single arm pilot study of Metformin in patients
with Fanconi Anemia (FA) and cytopenias with the primary endpoint of hematologic response.
This study will also assess safety, tolerability, and the biologic effects of Metformin in
patients with FA.
Phase:
Phase 2
Details
Lead Sponsor:
Boston Children's Hospital Boston Children’s Hospital