Overview

Phase III Trial of Sirolimus in IBM

Status:
Not yet recruiting
Trial end date:
2023-11-01
Target enrollment:
Participant gender:
Summary
The hypothesis is that Sirolimus, (Rapamycin (R)) which is currently used in organ transplantation and works by blocking the activity of T effector cells but preserving T regulatory cells, as well as by inducing autophagy (protein degradation), will be effective in IBM to slow or stabilize disease progression, helping to maintain patient function and independence. This phase III trial will confirm pilot data showing statistically significant clinical outcomes.
Phase:
Phase 3
Details
Lead Sponsor:
University of Kansas Medical Center
Collaborator:
The Perron Institute
Treatments:
Sirolimus