Overview

Phase II Open Label Study Using Triheptanoin in Patients With Glucose Type 1 Transporter Deficiency GLUT1-DS

Status:
Completed
Trial end date:
2019-07-04
Target enrollment:
Participant gender:
Summary
The purpose of this project is to study the efficacy of triheptanoin oil in patients with GLUT1 deficiency syndrome.
Phase:
Phase 2
Details
Lead Sponsor:
Institut National de la Santé Et de la Recherche Médicale, France
Collaborator:
Ultragenyx Pharmaceutical Inc