Phase 2a Pilot Study of NBMI Treatment in Patients With Beta Thalassemia Major, Requiring Iron Chelation
Status:
Completed
Trial end date:
2020-08-30
Target enrollment:
Participant gender:
Summary
A pilot study to explore safety and efficacy of NBMI treatment in patients with Beta
Thalassemia Major requiring iron chelation
Investigational product: NBMI (N1,N3-bis(2-mercaptoethyl) isophthalamide), INN: Emeramide
Indication: Beta Thalassemia Major