Overview

Phase 2 Tolerability and Effects of ALK-001 on Stargardt Disease

Status:
Recruiting
Trial end date:
2022-03-01
Target enrollment:
Participant gender:
Summary
The purpose of this study is to determine the long term safety and tolerability of ALK-001 (C20-D3-retinyl acetate), and to explore the effects of ALK-001 on the progression of Stargardt disease in patients between the ages of 8 and 70 years old. Funding Source - FDA OOPD
Phase:
Phase 2
Details
Lead Sponsor:
Alkeus Pharmaceuticals, Inc.
Treatments:
Retinol acetate
Vitamin A