Overview

PDE Inhibitors in DMD Study (Acute Dosing Study)

Status:
Completed
Trial end date:
1969-12-31
Target enrollment:
Participant gender:
Summary
PDE5A inhibition, which boosts NO-cGMP signaling, will relieve functional muscle ischemia and restore normal blood flow regulation (i.e., functional sympatholysis) during exercise in boys with DMD. The investigators specific aim is to perform an efficient dose-titration study to inform the design of a randomized multicenter trial of PDE5A inhibition for clinical skeletal muscle and cardiac endpoints.
Phase:
Phase 1
Details
Lead Sponsor:
Cedars-Sinai Medical Center
Treatments:
Sildenafil Citrate
Tadalafil