Oxandrolone for the Treatment of Bone Marrow Aplasia in Fanconi Anemia
Status:
Completed
Trial end date:
2010-01-01
Target enrollment:
Participant gender:
Summary
The purpose of this study is to evaluate the safety of the drug oxandrolone (a type of
androgen steroid) in patients with Fanconi anemia (FA), and to determine if this drug can
help in the treatment of bone marrow failure in these patients. Androgen steroids are male
hormones that can stimulate the production of red blood cells (the cells which carry oxygen
in the blood) and platelets (cells that help blood clot).