Overview

Midostaurin in Indolent Systemic Mastocytosis

Status:
Unknown status
Trial end date:
2015-05-01
Target enrollment:
Participant gender:
Summary
Rationale: Patients with indolent or smoldering systemic mastocytosis can have severe disabling symptoms. Almost all patients have fatigue, a compromised quality of life, hampering normal functioning. Because this form of mastocytosis is not considered life-threatening, mast cell eradication has never been applied and patients receive only symptomatic therapy with histamine blockers. Midostaurin, a c-KIT inhibitor has shown activity regarding symptom control and decrease of malignant mast cells in patients with aggressive systemic mastocytosis (ASM) or mast cell leukemia
Phase:
Phase 2
Details
Lead Sponsor:
University Medical Center Groningen
Treatments:
4'-N-benzoylstaurosporine
Midostaurin
Staurosporine