Long Term Beta Thalassemia Treatment: Findings From The Extension Period
Status:
ACTIVE_NOT_RECRUITING
Trial end date:
2025-07-01
Target enrollment:
Participant gender:
Summary
The project, titled "Long Term Beta Thalassemia Treatment: Findings From The Extension Period Of Phase 2 Clinical Trial," aims to compare the efficacy and safety of combination therapy (thalidomide and hydroxyurea) versus thalidomide alone. The study, lasting three years, is a Phase 2 single-center, open-label interventional study with a sample size of 30 participants aged 8-35 years. It includes specific inclusion and exclusion criteria for participant selection. Data will be collected through clinical interviews and medical records and analyzed using(Statistical Package for the Social Sciences. This project aims to enhance beta thalassemia treatment strategies, focusing on reducing transfusion dependency and improving patient quality of life.
Phase:
PHASE2
Details
Lead Sponsor:
National Institute of Blood and Marrow Transplant (NIBMT), Pakistan