Overview

Leniolisib for Immune Dysregulation in PIDs

Status:
RECRUITING
Trial end date:
2025-10-01
Target enrollment:
Participant gender:
Summary
This study is an exploratory, non-randomized, open-label, within-patient dose escalation study. The primary objective is to assess safety and tolerability of leniolisib. Secondary objectives include assessments of PK/PD, and to explore clinical efficacy measures with administration of three different dose levels of leniolisib.
Phase:
PHASE2
Details
Lead Sponsor:
Pharming Technologies B.V.
Treatments:
leniolisib