Overview

Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease

Status:
Recruiting
Trial end date:
2023-12-01
Target enrollment:
Participant gender:
Summary
Open-label, clinical trial of scAAV9.U1a.hSGSH injected intravenously through a peripheral limb vein
Phase:
Phase 1/Phase 2
Details
Lead Sponsor:
Abeona Therapeutics, Inc