First in Human SAD/MAD Safety and PK Study With Adult DMD Safety and PK Cohort
Status:
COMPLETED
Trial end date:
2025-04-28
Target enrollment:
Participant gender:
Summary
This is a first-in-human (FIH), Phase 1 study of orally administered SAT-3247 in healthy adult volunteers (HVs) and adult participants with DMD to determine safety, tolerability, pharmacokinetics and pharmacodynamics.