Overview

Fenfluramine in CDKL5 Deficiency Disorder (CDD)

Status:
Enrolling by invitation
Trial end date:
2022-04-01
Target enrollment:
Participant gender:
Summary
This study will be enrolling 10 patients, ages 2-18 years old, with a confirmed genetic/clinical diagnosis of CDKL5 Deficiency Disorder (CDD) in an open label trial of fenfluramine for seizure control. Patients will be titrated over 14 days to a dose of ZX008 0.8 mg/kg/day (maximum dose 30 mg/d).
Phase:
Phase 2
Details
Lead Sponsor:
New York University School of Medicine
NYU Langone Health
Treatments:
Fenfluramine