Overview

Evaluation of Salbutamol as an Adjuvant Therapy for Pompe Disease

Status:
Completed
Trial end date:
2016-06-01
Target enrollment:
Participant gender:
Summary
evaluate if beta 2-adrenergic agonist can have adjuvant effect to patients with infantile-onset Pompe disease under enzyme replacement therapy
Phase:
Phase 4
Details
Lead Sponsor:
National Taiwan University Hospital
Treatments:
Albuterol