Overview

Evaluation of BH4 Responsiveness in Our PKU Patients

Status:
ACTIVE_NOT_RECRUITING
Trial end date:
2026-09-01
Target enrollment:
Participant gender:
Summary
This study aims to evaluate BH4 responsiveness in our PKU patients and to correlate BH4 responsiveness with their genotype
Phase:
PHASE1
Details
Lead Sponsor:
Sohag University
Treatments:
sapropterin