Overview

Efficacy and Safety of Pirfenidone Treatment in HPS-ILD

Status:
Not yet recruiting
Trial end date:
2022-12-31
Target enrollment:
Participant gender:
Summary
This research study will explore the safety and efficacy of the drug, pirfenidone, in patients with a diagnosis of Hermansky-Pudlak Syndrome (HPS) who have an associated interstitial lung disease (ILD) over a planned period of 56 weeks.
Phase:
Phase 2
Details
Lead Sponsor:
Jesse Roman
Collaborator:
Genentech, Inc.
Treatments:
Pirfenidone