Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome
Status:
Recruiting
Trial end date:
2022-01-31
Target enrollment:
Participant gender:
Summary
This trial aims to investigate the efficacy, safety and tolerability of sodium valproate in
the treatment of patients with Wolfram syndrome. 70 paediatric and adult patients will be
randomised 2:1 to receive either sodium valproate or placebo at 6 international centres.