Overview

Efficacy, Safety, Pharmacokinetics and Pharmacodynamics Study, Assessing Multiple LNP023 Doses in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria

Status:
Active, not recruiting
Trial end date:
2022-03-21
Target enrollment:
Participant gender:
Summary
The main purpose of this study is to evaluate the efficacy of LNP023 in patients with PNH, showing signs of active hemolysis.
Phase:
Phase 2
Details
Lead Sponsor:
Novartis Pharmaceuticals