Overview

Effect of Oral Cimetidine in the Protoporphyrias

Status:
Not yet recruiting
Trial end date:
2025-09-01
Target enrollment:
Participant gender:
Summary
Erythropoietic protoporphyria (EPP) and X-linked protoporphyria (XLP) result from genetic defects of heme biosynthesis that cause life-long, painful cutaneous sensitivity to light. The objective of this study is to determine the efficacy and safety of oral cimetidine administration for treatment of the protoporphyrias. Efficacy will be based on protoporphyrin levels, photosensitivity, and quality of life questionnaires.
Phase:
Phase 2
Details
Lead Sponsor:
Amy K. Dickey, M.D.
Collaborator:
University of Texas
Treatments:
Cimetidine