Overview

Early Diagnosis and Stem Cell Transplantation for Severe Immunodeficiency Diseases

Status:
Unknown status
Trial end date:
2017-12-01
Target enrollment:
Participant gender:
Summary
The hypothesis of this study is that children with severe primary immunodeficiencies will benefit from early stem cell transplantation utilizing a reduced intensity conditioning regimen. This regimen is associated with a low risk of complications and will lead to correction of the underlying immunological defects.
Phase:
Phase 2
Details
Lead Sponsor:
Ann & Robert H Lurie Children's Hospital of Chicago
Treatments:
Antilymphocyte Serum
Busulfan
Fludarabine
Fludarabine phosphate