Clinical Benefit, Safety, PK and PD Study of AT-007 in Pediatric Subjects With Classic Galactosemia
Status:
Recruiting
Trial end date:
2023-06-01
Target enrollment:
Participant gender:
Summary
This study is designed to assess the clinical benefit as well as the safety, pharmacokinetics
(PK), and pharmacodynamics (PD) (reduction of galactitol levels) of AT-007 in pediatric
subjects with Classic Galactosemia (CG).