CARNIVAL Type I: Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy (SMA) Type I
Status:
Completed
Trial end date:
2012-06-01
Target enrollment:
Participant gender:
Summary
This is a multi-center trial to test safety and evaluate early treatment intervention with
valproic acid and carnitine in moderating SMA symptoms of Type I infants.
Phase:
Phase 1/Phase 2
Details
Lead Sponsor:
University of Utah
Collaborators:
Families of Spinal Muscular Atrophy Leadiant Biosciences, Inc. Sigma Tau Pharmaceuticals, Inc.