The purpose of this study is to determine whether bezafibrate is effective in the treatment
of the muscular adult form of carnitine palmitoyltransferase 2 deficiency
Phase:
Phase 3
Details
Lead Sponsor:
Assistance Publique - Hôpitaux de Paris
Collaborators:
Association Française contre les Myopathies (AFM), Paris Institut National de la Santé Et de la Recherche Médicale, France