Overview

An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.

Status:
Recruiting
Trial end date:
2029-02-20
Target enrollment:
Participant gender:
Summary
This early Phase trial is to prove the safety and efficacy of VGN-R09b to treat patients with AADC deficiency.
Phase:
Early Phase 1
Details
Lead Sponsor:
Shanghai Jiao Tong University School of Medicine
Collaborator:
Shanghai Vitalgen BioPharma Co., Ltd.