Allogeneic Hematopoietic Stem Cell Transplant For Epidermolysis Bullosa
Status:
Terminated
Trial end date:
2011-08-01
Target enrollment:
Participant gender:
Summary
RATIONALE: In animal models, stem cells have been shown to home to the skin and repair the
biochemical and structural abnormalities associated with recessive dystrophic epidermolysis
bullosa (RDEB) (collagen 7 deficiency).
PURPOSE: To determine the safety and effectiveness of stem cell infusion in the treatment of
RDEB.