Overview

Alipogene Tiparvovec for the Treatment of LPLD Patients

Status:
Withdrawn
Trial end date:
2020-09-01
Target enrollment:
Participant gender:
Summary
The aim of the study is to provide further confirmatory evidence of clinical benefit in LPLD patients treated with alipogene tiparvovec by assessing both the "clinical response" (as defined by a range of parameters), and "the metabolic response" (postprandial CM metabolism) in LPLD patients with and without an immunosuppressant regimen.
Phase:
Phase 2
Details
Lead Sponsor:
UniQure Biopharma B.V.
Collaborator:
Chiesi Farmaceutici S.p.A.
Treatments:
Cyclosporine
Cyclosporins
Methylprednisolone
Methylprednisolone acetate
Methylprednisolone Hemisuccinate
Mycophenolate mofetil
Mycophenolic Acid
Prednisolone
Prednisolone acetate
Prednisolone hemisuccinate
Prednisolone phosphate